Working with the Pharma Industry

TREAT-NMD brings together the key players in the neuromuscular field and is a natural partner to support biotech and pharmaceutical companies in developing new therapeutics for neuromuscular conditions.

We provide a range of services to support including;

• Comprehensive, disease specific datasets in SMA, DMD, LGMD to better inform on the natural history of neuromuscular diseases These datasets capture high quality data to support post-marketing surveillance (safety and effectiveness) for new treatments
• Global Registry Enquiries can be requested by industry, regulators, patient organisations or academia into the network in order to support clinical trial feasibility, academic research, trial recruitment, or other research needs.
• Global Registry Platform a secure data sharing mechanism which will support natural history studies and provide anonymised patient-level data and aggregate data for research purposes.
• TREAT-NMD Advisory committee for therapeutics to provide guidance on the translation and development path of therapeutics programs in rare neuromuscular diseases with large unmet need 
• Education services including masterclasses, workshops and seminars with a goal to accelerate diagnosis through providing expert input on diagnosis, standards of care and emerging therapies