Current trials in SMA
TREAT-NMD is working closely with the pharmaceutical companies planning trials in neuromuscular diseases. The resources and expertise available through the network can make it much easier for companies to do trials, and many of the doctors involved in the network are principal investigators for the trials that are currently ongoing.
Nevertheless, we cannot ourselves keep an up-to-date overview of all the trials that are currently happening across the world. The most comprehensive online listing of trials is at clinicaltrials.gov – companies are obliged to provide details of their trials there.
The table below lists all SMA trials registered or updated on clinicaltrials.gov in the last 1000 days. Because it links directly to clinicaltrials.gov it is automatically updated whenever the information on clinicaltrials.gov changes.
Please note that TREAT-NMD can take no responsibility for the accuracy of the information below, which is pulled directly from clinicaltrials.gov.
Trials for SMA listed on clinicaltrials.gov
- Spinal Cord Stimulation in Spinal Muscular Atrophy
- Exoskeleton Impact on the Quality of Life on Patients With Spinal Muscular Atrophy
- Schulze Muscular Dystrophy Ability Clinical Study
- Phase IIIb, Open-label, Multi-center Study to Evaluate Safety, Tolerability and Efficacy of OAV101 Administered Intrathecally to Participants With SMA Who Discontinued Treatment With Nusinersen or Risdiplam
- Quality of Life and Participation of the Adult With Spinal Muscular Atrophy in France
- Virtual Reality for the Mitigation of Anxiety During Intrathecal Administration in Participants With Spinal Muscular Atrophy
- Hippotherapy in Children With Spinal Muscular Atrophy
- A Study to Evaluate the Efficacy and Safety of Taldefgrobep Alfa in Participants With Spinal Muscular Atrophy
- Long-term Follow-Up of Patients With Spinal Muscular Atrophy Treated With OAV101 in Clinical Trials
- A Randomized, Double-Blind, Placebo-Controlled Study to Evaluate the Efficacy and Safety of Taldefgrobep Alfa in Participants With Spinal Muscular Atrophy
- Procedural Sedation for Pediatric Patients With Spinal Muscular Atrophy
- Pompe & Pain - Study to Assess Nociceptive Pain in Adult Patients With Pompe Disease
- Pompe & Pain - Study to Assess Nociceptive Pain in Adult Patients With Pompe Disease
- Long-Term Follow-Up Study of Risdiplam in Participants With Spinal Muscular Atrophy (SMA)
- Investigating NMJ Defects in SMA Following Central and Peripheral SMN Restoration