For clinicians and researchers, lack of support tools such as validated clinical outcome measures or standard operating procedures for research protocols has held back therapeutic development. Whilst for patients, promising research results
have still not been translated into the treatments they hope for.
Strong collaborations have been built across the neuromuscular community by engaging numerous international researchers and organizations worldwide, who are able to tap into the resources developed by TREAT-NMD. The resources provided in this section of our site span the research and clinical arenas and are part of a whole suite of tools that are essential for rapid progress towards new therapies.