Director, Center for Gene Therapy & Professor of Pediatrics, Neurology & Pathology
United States of America
Jerry is the Director of the Centre for Gene Therapy and a Professor of Pediatrics, Neurology, and Pathology with extensive experience in translational neuromuscular disease research including clinical trials. He completed his residency in Neurology at the Neurological Institute at Columbia University, and trained in neuromuscular disease at the Medical Branch of Neurology at NIH.
He chaired the Department of Neurology at Ohio State University before moving into his current position at Children’s Hospital. He was a founding member of the collaborative CIDD Muscle Group. This Group contributed in multiple ways to DMD including insight into the natural history, the development of outcome measures for clinical trials, and establishing the efficacy for corticosteroid treatment. His use of molecular tools to potentially treat neuromuscular disease best describes his current area of interest and expertise.
In his current position, he provides leadership for a talented group of investigators engaged in translational research inclusive of gene therapy (novel approaches to gene manipulation and delivery), clinical trials (gene replacement, gene restoration, pharmacologic manipulation) and clinical characterization (genotype – phenotype correlations) of neuromuscular disease.